The treatment landscape for bleeding disorders is changing
It is an exciting time in gene and emerging therapies for bleeding disorders in Australia. The aim of the Gene & Emerging Therapies (GETs) hub is to give the bleeding disorders community up-to-date information and knowledge about all these different treatments and to help make a shared decision with family and your HTC as they become available.
Gene therapy
Other new and emerging treatments
Making decisions about treatment
Information for health professionals (coming soon)
Resources
HFA Gene Therapy Snapshot Survey
HFA would like to understand what our community members want from their haemophilia treatments and your perspectives on gene therapy in particular.
Gene therapy
Gene therapy for haemophilia Information for people with haemophilia about gene therapy and how it works in haemophilia. This booklet explains the types of gene therapy that are being trialled in haemophilia at present, who...
ISTH 2024 Congress: novel therapies
Exciting new haemophilia treatments using a range of innovative technologies were highlighted at ISTH 2024 Congress.
New Therapies Webinar
Dr Liane Khoo (Haematologist and HTC Director, Royal Prince Alfred Hospital), Dr Sally Campbell (Haematologist, and acting HTC Director, Royal Brisbane & Women’s Hospital), Stephen Matthews (Clinical Nurse Consultant, HTC, Royal Prince Alfred Hospital) and Sharon...
Gene therapy FAQs
Is gene therapy a cure for haemophilia? In many cases successful gene therapy means that a person with severe haemophilia now has mild haemophilia, although a small number now have normal factor levels. It is...
New haemophilia therapies
ALEX KLEVER Alex Klever is Clinical Nurse Consultant – Haemophilia at the Queensland Haemophilia Centre, Royal Brisbane & Women’s Hospital Plenary – Treatment landscape into the future Chair ~ David FaganFrom then to now ~...
Have your gene therapy questions answered
Dr Michiel Coppens is coming to Australia and we want your questions for a special ‘Ask Me Anything’ interview about gene therapy.
Gene Therapy Interview with Dr Michiel Coppens
In this interview chaired by Dr Stephanie P’ng and led by questions from the community, Dr Michiel Coppens explains what gene therapy is, how it works, and how it can be used to treat people...
Gene therapy interview with Dr Michiel Coppens now available
On 14 May 2024 we were fortunate to have Dr Michiel Coppens join us at the HFA office for an interview about gene therapy. Watch it now.
Gene therapy webinar
Dr Michiel Coppens joined us at HFA for an interview about gene therapy, answering questions from the community. Watch the video or read the transcript.
Congress – a Foundation perspective
Haemophilia Foundation Australia President Gavin Finkelstein spoke with HFA about his experiences at the WFH 2024 World Congress.
New gene therapy resource
HFA’s new resource Gene therapy for haemophilia was developed to answer the questions from our community: What types of gene therapy are used in haemophilia? How does gene therapy work? Is it a cure?...
From the President
Heading to the end of the year, we review our progress. Gene and emerging therapies are on the agenda, and Bleeding Disorders Awareness Month is coming up.
Haemophilia – the spice of life
Willem spoke to us about working, exercising and being out and about in these days with new treatments.
Gene therapy
Gene therapy for haemophilia has been in advanced clinical trials for some years now and this Congress was a timely forum to discuss and evaluate it critically. ROBYN SHOEMARK Robyn Shoemark is Clinical Nurse Consultant...
Haemophilia gene therapy snapshot survey
HFA’s haemophilia gene therapy snapshot survey asked people and parents of children with haemophilia what outcomes they would like from treatment now and in the future.
How changing treatments has changed Scott’s world
Scott shares how changes to his haemophilia treatment have made it possible for him to do more.
Novel haemophilia therapies
Living in the new world of novel haemophilia therapies ROBYN SHOEMARK Robyn Shoemark is Clinical Nurse Consultant Haemophilia/Haematology at the Kids Factor Zone, The Children’s Hospital at Westmead, Sydney, NSW Discussion about the impact of...
World Hepatitis Day 2024
World Hepatitis Day 2024 reminds us It’s time for action – hepatitis C and liver health remain important issues for our community and acting now is vital.
New developments in haemophilia nursing
The EAHAD Congress was a stimulating forum to discuss new issues in haemophilia nursing – eg, bleeds with new therapies, women and mild haemophilia.
Acknowledgments
The Gene and Emerging Therapies Hub has been funded by education grants from CSL Behring and Sanofi. This funding is based on a mutual understanding that HFA will act independently for the benefit of the bleeding disorders community. HFA does not promote any particular pharmaceutical product. Where possible products are referred to by their class or generic name and any mention of any commercial brand is strictly for educational purposes.