The treatment landscape for bleeding disorders is changing
It is an exciting time in gene and emerging therapies for bleeding disorders in Australia. The aim of the Gene & Emerging Therapies (GETs) hub is to give the bleeding disorders community up-to-date information and knowledge about all these different treatments and to help make a shared decision with family and your HTC as they become available.
Gene therapy
Other new and emerging treatments
Making decisions about treatment
Information for health professionals (coming soon)
Resources
Gene therapy
Gene therapy for haemophilia Information for people with haemophilia about gene therapy and how it works in haemophilia. This booklet explains the types of gene therapy that are being trialled in haemophilia at present, who...
Gene and emerging therapies in haemophilia
Exciting advancements in gene therapy and other emerging treatments for haemophilia were presented at the Blood 2024 conference.
ISTH 2024 Congress: novel therapies
Exciting new haemophilia treatments using a range of innovative technologies were highlighted at ISTH 2024 Congress.
WFH Summit: new therapies and approaches
WFH CCS topics included health literacy in shared decision-making, new therapies for VWD and women and girls with bleeding disorders.
Haemophilia gene therapy snapshot survey
HFA’s haemophilia gene therapy snapshot survey asked people and parents of children with haemophilia what outcomes they would like from treatment now and in the future.
Haemophilia Treatment Preferences Survey
(HaemPref Survey) How do individuals make decisions about treatment? What factors encourage or discourage patients from treatments? What are individuals’ treatment goals? Results presented are based on a study conducted by Community and Patient Preference...
Jack’s latest travel adventures
Jack talks about his travel adventures in Canada and the USA, snowboarding and managing haemophilia on the road with new treatments.
Haemophilia treatment survey
SUZANNE O'CALLAGHAN Suzanne O'Callaghan is HFA Policy Research and Education Manager What information does our community want about new haemophilia treatments? And for those who are affected, what would you like haemophilia treatment to achieve...
Gene therapy FAQs
Is gene therapy a cure for haemophilia? In many cases successful gene therapy means that a person with severe haemophilia now has mild haemophilia, although a small number now have normal factor levels. It is...
From the President
So much is happening and changing very quickly – hepatitis C, women and girls, the conference and new therapies.
New Therapies Webinar
Dr Liane Khoo (Haematologist and HTC Director, Royal Prince Alfred Hospital), Dr Sally Campbell (Haematologist, and acting HTC Director, Royal Brisbane & Women’s Hospital), Stephen Matthews (Clinical Nurse Consultant, HTC, Royal Prince Alfred Hospital) and Sharon...
New haemophilia therapies
ALEX KLEVER Alex Klever is Clinical Nurse Consultant – Haemophilia at the Queensland Haemophilia Centre, Royal Brisbane & Women’s Hospital Plenary – Treatment landscape into the future Chair ~ David FaganFrom then to now ~...
Gene therapy interview with Dr Michiel Coppens now available
On 14 May 2024 we were fortunate to have Dr Michiel Coppens join us at the HFA office for an interview about gene therapy. Watch it now.
ISTH 2025 – emerging therapies in haemophilia and VWD
At ISTH 2025 researchers shared advances in emerging therapies for haemophilia and von Willebrand disease (VWD).
Gene Therapy Interview with Dr Michiel Coppens
In this interview chaired by Dr Stephanie P’ng and led by questions from the community, Dr Michiel Coppens explains what gene therapy is, how it works, and how it can be used to treat people...
Gene therapy webinar
Dr Michiel Coppens joined us at HFA for an interview about gene therapy, answering questions from the community. Watch the video or read the transcript.
Congress – a Foundation perspective
Haemophilia Foundation Australia President Gavin Finkelstein spoke with HFA about his experiences at the WFH 2024 World Congress.
Haemophilia – the spice of life
Willem spoke to us about working, exercising and being out and about in these days with new treatments.
New gene therapy resource
HFA’s new resource Gene therapy for haemophilia was developed to answer the questions from our community: What types of gene therapy are used in haemophilia? How does gene therapy work? Is it a cure?...
From the President
Heading to the end of the year, we review our progress. Gene and emerging therapies are on the agenda, and Bleeding Disorders Awareness Month is coming up.
Acknowledgments
The Gene and Emerging Therapies Hub has been funded by education grants from CSL Behring and Sanofi. This funding is based on a mutual understanding that HFA will act independently for the benefit of the bleeding disorders community. HFA does not promote any particular pharmaceutical product. Where possible products are referred to by their class or generic name and any mention of any commercial brand is strictly for educational purposes.