New gene therapy resource

HFA’s new resource Gene therapy for haemophilia was developed to answer the questions from our community:

  • What types of gene therapy are used in haemophilia?
  • How does gene therapy work?
  • Is it a cure?
  • How safe is it?
  • Who can have gene therapy?

 Gene therapy for haemophilia
The information includes diagrams to explain simply how genes and gene therapy work.
Our thanks to the bleeding disorders community members and expert reviewers and our designer, Ray Hehr, who made valuable contributions to this resource.
This resource was funded by an education grant from BioMarin.
Gene therapy for haemophilia is available on the HFA website and in print. A print copy was posted out with the December issue of National Haemophilia. To order print copies, contact HFA:
T: 1800 807 173

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