The treatment landscape for bleeding disorders is changing
It is an exciting time in gene and emerging therapies for bleeding disorders in Australia. The aim of the Gene & Emerging Therapies (GETs) hub is to give the bleeding disorders community up-to-date information and knowledge about all these different treatments and to help make a shared decision with family and your HTC as they become available.
Gene therapy
Other new and emerging treatments
Making decisions about treatment
Information for health professionals (coming soon)
Resources
Gene therapy
Gene therapy for haemophilia Information for people with haemophilia about gene therapy and how it works in haemophilia. This booklet explains the types of gene therapy that are being trialled in haemophilia at present, who...
HFA Gene Therapy Snapshot Survey
HFA would like to understand what our community members want from their haemophilia treatments and your perspectives on gene therapy in particular.
Gene therapy
Gene therapy for haemophilia has been in advanced clinical trials for some years now and this Congress was a timely forum to discuss and evaluate it critically. ROBYN SHOEMARK Robyn Shoemark is Clinical Nurse Consultant...
Haemophilia gene therapy snapshot survey
HFA’s haemophilia gene therapy snapshot survey asked people and parents of children with haemophilia what outcomes they would like from treatment now and in the future.
MyABDR and recording your treatment
With new haemophilia treatments, recording on MyABDR has some challenges. HTCs and users share their tips.
Novel haemophilia therapies
Living in the new world of novel haemophilia therapies ROBYN SHOEMARK Robyn Shoemark is Clinical Nurse Consultant Haemophilia/Haematology at the Kids Factor Zone, The Children’s Hospital at Westmead, Sydney, NSW Discussion about the impact of...
World Hepatitis Day 2024
World Hepatitis Day 2024 reminds us It’s time for action – hepatitis C and liver health remain important issues for our community and acting now is vital.
Jack’s latest travel adventures
Jack talks about his travel adventures in Canada and the USA, snowboarding and managing haemophilia on the road with new treatments.
New haemophilia therapies
It is an exciting time with more new haemophilia treatments likely to become available in Australia, but there have been a lot of questions about them and what they will mean for treatment and care....
From the President
As we wrap up 2024, HFA reflects on our achievements in new therapies, hep C advocacy and support during the year.
ISTH 2024 Congress: novel therapies
Exciting new haemophilia treatments using a range of innovative technologies were highlighted at ISTH 2024 Congress.
Haemophilia treatment survey
SUZANNE O'CALLAGHAN Suzanne O'Callaghan is HFA Policy Research and Education Manager What information does our community want about new haemophilia treatments? And for those who are affected, what would you like haemophilia treatment to achieve...
Gene therapy FAQs
Is gene therapy a cure for haemophilia? In many cases successful gene therapy means that a person with severe haemophilia now has mild haemophilia, although a small number now have normal factor levels. It is...
Have your gene therapy questions answered
Dr Michiel Coppens is coming to Australia and we want your questions for a special ‘Ask Me Anything’ interview about gene therapy.
New Therapies Webinar
Dr Liane Khoo (Haematologist and HTC Director, Royal Prince Alfred Hospital), Dr Sally Campbell (Haematologist, and acting HTC Director, Royal Brisbane & Women’s Hospital), Stephen Matthews (Clinical Nurse Consultant, HTC, Royal Prince Alfred Hospital) and Sharon...
Gene therapy interview with Dr Michiel Coppens now available
On 14 May 2024 we were fortunate to have Dr Michiel Coppens join us at the HFA office for an interview about gene therapy. Watch it now.
New haemophilia therapies
ALEX KLEVER Alex Klever is Clinical Nurse Consultant – Haemophilia at the Queensland Haemophilia Centre, Royal Brisbane & Women’s Hospital Plenary – Treatment landscape into the future Chair ~ David FaganFrom then to now ~...
Gene Therapy Interview with Dr Michiel Coppens
In this interview chaired by Dr Stephanie P’ng and led by questions from the community, Dr Michiel Coppens explains what gene therapy is, how it works, and how it can be used to treat people...
Gene therapy webinar
Dr Michiel Coppens joined us at HFA for an interview about gene therapy, answering questions from the community. Watch the video or read the transcript.
Haemophilia – the spice of life
Willem spoke to us about working, exercising and being out and about in these days with new treatments.
Acknowledgments
The Gene and Emerging Therapies Hub has been funded by education grants from CSL Behring and Sanofi. This funding is based on a mutual understanding that HFA will act independently for the benefit of the bleeding disorders community. HFA does not promote any particular pharmaceutical product. Where possible products are referred to by their class or generic name and any mention of any commercial brand is strictly for educational purposes.